OS Therapies receives positive FDA feedback for osteosarcoma treatment

Published 24/06/2025, 12:50
OS Therapies receives positive FDA feedback for osteosarcoma treatment

NEW YORK - OS Therapies (NYSE-A:OSTX), a clinical-stage biotech company with a current market capitalization of approximately $48 million, announced Tuesday it has received positive feedback from the U.S. Food and Drug Administration regarding its Phase 2b trial of OST-HER2, a treatment for pediatric lung metastatic osteosarcoma.

The company has submitted requests for an End of Phase 2 Meeting and Breakthrough Therapy Designation based on the FDA’s feedback from a Type D Meeting held in mid-June. The End of Phase 2 Meeting is expected to take place in the third quarter of 2025. Despite the positive regulatory developments, InvestingPro data shows the stock has declined over 55% in the past six months, though analysts maintain price targets ranging from $6 to $20.

"We are pleased with the feedback we received from the FDA regarding the use of external control comparators in settings where placebo-controlled randomization trials are not feasible," said Dr. Robert Petit, Chief Medical & Scientific Officer of OS Therapies, according to a press release statement.

The FDA provided input on statistical methods for comparing OST-HER2 treatment with external control arms to support a Biologics Licensing Application through the Accelerated Approval Program.

OST-HER2 has received Rare Pediatric Disease Designation for osteosarcoma from the FDA. If it receives conditional approval via Accelerated Review before September 30, 2026, it will become eligible for a Priority Review Voucher, which the company intends to sell. The most recent such voucher sold for $160 million in June 2025.

The immunotherapy uses a HER2-bioengineered form of the bacterium Listeria monocytogenes to trigger an immune response against HER2-expressing cancer cells. The company’s Phase 2b trial demonstrated statistically significant benefit in the 12-month event-free survival primary endpoint.

OS Therapies anticipates submitting a Biologics Licensing Application to the FDA for OST-HER2 in osteosarcoma in 2025.

The osteosarcoma treatment market was estimated at $1.2 billion in 2022, according to data cited in the company’s announcement. While the company maintains a GOOD financial health score according to InvestingPro analysis, it reported negative EBITDA of $11.2 million in the last twelve months. Subscribers to InvestingPro can access additional financial metrics and 6 more exclusive ProTips about OSTX’s performance and outlook.

In other recent news, OS Therapies Inc. has announced multiple developments regarding its cancer drug OST-HER2. The company has requested the U.S. Food and Drug Administration (FDA) grant Regenerative Medicine Advanced Therapy (RMAT) Designation for OST-HER2, which could expedite its review process. Additionally, OS Therapies has secured a patent extending protection for its Listeria monocytogenes cancer immunotherapy platform until 2040, covering several pipeline candidates, including OST-HER2. The FDA is set to review a surrogate endpoint for OST-HER2, potentially leading to Breakthrough Therapy Designation and Accelerated Approval. OS Therapies has also partnered with EVERSANA to commercialize OST-HER2 in the U.S., leveraging EVERSANA’s integrated commercialization model to enhance market access. Furthermore, the company has received shareholder approval for a significant stock issuance, which could increase financial flexibility. These recent developments underscore OS Therapies’ strategic efforts to advance its pipeline and strengthen its market position.

This article was generated with the support of AI and reviewed by an editor. For more information see our T&C.

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