GEN Pharmaceuticals reports positive phase 1 results for Alzheimer’s drug

Published 28/07/2025, 13:02
GEN Pharmaceuticals reports positive phase 1 results for Alzheimer’s drug

ANKARA - GEN Pharmaceuticals (GENIL.IS), a Turkish specialty pharmaceutical company, announced Monday that its investigational drug candidate SUL-238 demonstrated positive results in a Phase 1 clinical trial for Alzheimer’s and other neurodegenerative diseases.

The first-in-human trial evaluated the safety, tolerability, and pharmacokinetics of the orally administered mitochondria-directed drug in 53 healthy elderly volunteers across three study parts.

According to the company’s press release, single oral doses ranging from 50-2000 mg were found to be safe and well-tolerated, with adverse event rates comparable between SUL-238 and placebo. All reported adverse events were mild or moderate, with none limiting dose escalation.

The drug demonstrated a favorable pharmacokinetic profile with a mean terminal elimination half-life of 0.86-3.80 hours. The company reported that SUL-238 showed high brain penetration, with cerebrospinal fluid-to-plasma percentages at 2 and 8 hours post-dose of 21.1% and 74.2%, respectively.

Under fed conditions, the maximum plasma concentration and area under the plasma concentration-time curve decreased by 50% and 60%, respectively.

SUL-238 is described as a hibernation-derived small molecule that targets mitochondria, supporting cellular energy production through complex I/IV activation. The drug has shown improved mitochondrial function in rodent models of various diseases, including neurodegenerative conditions.

GEN Pharmaceuticals licenses SUL-238 from Dutch biotech company Sulfateq BV for neurodegenerative disease applications.

The findings were presented at the Alzheimer’s Association International Conference 2025 in Toronto.

Based on these results, the company plans to advance SUL-238 into further clinical development for Alzheimer’s and other neurodegenerative diseases.

This article was generated with the support of AI and reviewed by an editor. For more information see our T&C.

Latest comments

Risk Disclosure: Trading in financial instruments and/or cryptocurrencies involves high risks including the risk of losing some, or all, of your investment amount, and may not be suitable for all investors. Prices of cryptocurrencies are extremely volatile and may be affected by external factors such as financial, regulatory or political events. Trading on margin increases the financial risks.
Before deciding to trade in financial instrument or cryptocurrencies you should be fully informed of the risks and costs associated with trading the financial markets, carefully consider your investment objectives, level of experience, and risk appetite, and seek professional advice where needed.
Fusion Media would like to remind you that the data contained in this website is not necessarily real-time nor accurate. The data and prices on the website are not necessarily provided by any market or exchange, but may be provided by market makers, and so prices may not be accurate and may differ from the actual price at any given market, meaning prices are indicative and not appropriate for trading purposes. Fusion Media and any provider of the data contained in this website will not accept liability for any loss or damage as a result of your trading, or your reliance on the information contained within this website.
It is prohibited to use, store, reproduce, display, modify, transmit or distribute the data contained in this website without the explicit prior written permission of Fusion Media and/or the data provider. All intellectual property rights are reserved by the providers and/or the exchange providing the data contained in this website.
Fusion Media may be compensated by the advertisers that appear on the website, based on your interaction with the advertisements or advertisers
© 2007-2025 - Fusion Media Limited. All Rights Reserved.