Tenaya completes enrollment in both dose cohorts for HCM gene therapy

Published 30/07/2025, 14:08
Tenaya completes enrollment in both dose cohorts for HCM gene therapy

SOUTH SAN FRANCISCO - Tenaya Therapeutics, Inc. (NASDAQ:TNYA), a clinical-stage biotech with a current market capitalization of $114.5 million, has completed enrollment in both dose cohorts of its MyPEAK-1 Phase 1b/2 clinical trial for TN-201, a gene therapy targeting hypertrophic cardiomyopathy (HCM), the company announced Wednesday. According to InvestingPro data, the company maintains a strong liquidity position with a current ratio of 6.68, indicating robust short-term financial stability.

The biotech firm also reported dosing the first patient in Cohort 2 of its RIDGE-1 Phase 1b clinical trial of TN-401 for arrhythmogenic right ventricular cardiomyopathy (ARVC).

Independent Data Safety and Monitoring Boards (DSMBs) for both trials have endorsed proceeding per protocol, indicating favorable tolerability profiles for both gene therapies.

"Safety is paramount, and this milestone reinforces the favorable tolerability profile emerging for both TN-201 and TN-401," said Whit Tingley, Tenaya’s Chief Medical Officer, in a press release statement.

Initial data from the first three patients receiving TN-201 at the 3E13 vg/kg dose level showed the therapy reached cardiomyocytes with robust RNA expression. Increased MyBP-C protein levels were observed in two patients with serial biopsies. All three patients achieved New York Heart Association Class I post-treatment, indicating resolution of heart failure symptoms.

For the RIDGE-1 trial, the DSMB reviewed available data and endorsed dose escalation to the 6E13 vg/kg level while allowing expansion of Cohort 1 enrollment. The company has already dosed the first patient in the higher dose cohort.

Tenaya expects to report follow-up data from MyPEAK-1 Cohort 1 and initial data from Cohort 2 in the fourth quarter of 2025. Initial data from RIDGE-1 Cohort 1 is also expected in the fourth quarter, focusing on safety, tolerability, and cardiac biopsy analyses.

Both TN-201 and TN-401 have received Fast Track and Orphan Drug Designations from the U.S. Food and Drug Administration.

This article was generated with the support of AI and reviewed by an editor. For more information see our T&C.

Latest comments

Risk Disclosure: Trading in financial instruments and/or cryptocurrencies involves high risks including the risk of losing some, or all, of your investment amount, and may not be suitable for all investors. Prices of cryptocurrencies are extremely volatile and may be affected by external factors such as financial, regulatory or political events. Trading on margin increases the financial risks.
Before deciding to trade in financial instrument or cryptocurrencies you should be fully informed of the risks and costs associated with trading the financial markets, carefully consider your investment objectives, level of experience, and risk appetite, and seek professional advice where needed.
Fusion Media would like to remind you that the data contained in this website is not necessarily real-time nor accurate. The data and prices on the website are not necessarily provided by any market or exchange, but may be provided by market makers, and so prices may not be accurate and may differ from the actual price at any given market, meaning prices are indicative and not appropriate for trading purposes. Fusion Media and any provider of the data contained in this website will not accept liability for any loss or damage as a result of your trading, or your reliance on the information contained within this website.
It is prohibited to use, store, reproduce, display, modify, transmit or distribute the data contained in this website without the explicit prior written permission of Fusion Media and/or the data provider. All intellectual property rights are reserved by the providers and/or the exchange providing the data contained in this website.
Fusion Media may be compensated by the advertisers that appear on the website, based on your interaction with the advertisements or advertisers
© 2007-2025 - Fusion Media Limited. All Rights Reserved.