Mirum Pharmaceuticals, Inc., a biopharmaceutical company, focuses on the development and commercialization of novel therapies for debilitating rare and orphan diseases. Its lead product candidate is LIVMARLI (maralixibat), an orally administered and minimally absorbed ileal bile acid transporter (IBAT) inhibitor that is approved for the treatment of cholestatic pruritus in patients with Alagille syndrome in the United States and internationally. The company is also involved in the commercialization of Cholbam, a cholic acid capsule, which is approved as treatment for pediatric and adult patients with bile acid synthesis disorders due to single enzyme defects and for adjunctive treatment of patients with peroxisomal disorders, including peroxisome biogenesis disorder-Zellweger spectrum disorder and Smith-Lemli-Opitz syndrome; and Chenodal, a tablet, which is approved for the treatment of radiolucent stones in the gallbladder, and under Phase 3 development for the treatment cerebrotendinous xanthomatosis. In addition, it develops Volixibat, an oral and minimally absorbed agent designed to inhibit IBAT, currently under Phase 2b clinical trial for the treatment of adult patients with cholestatic liver diseases. The company was incorporated in 2018 and is headquartered in Foster City, California.
Rare Disease Pionee | Mirum Pharmaceuticals secures FDA approval for Ctexli, the first treatment for cerebrotendinous xanthomatosis in the US, bolstering its rare liver disease portfolio |
Financial Momentum | Q4 2024 revenues hit $99 million, contributing to full-year revenue of $336 million, an 81% year-over-year growth, with 2025 guidance set at $420-$435 million |
Pipeline Potential | Explore Mirum's promising pipeline, including volixibat for PSC and PBC, and MRM3379 for Fragile X Syndrome, representing billion-dollar market opportunities |
Market Valuation | Analysts maintain a bullish stance with a consensus recommendation of 1.4, and a price target of $74, reflecting confidence in Mirum's growth trajectory |
Metrics to compare | MIRM | Sector Sector - Average of metrics from a broad group of related Healthcare sector companies | Relationship RelationshipMIRMPeersSector | |
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P/E Ratio | −33.3x | −1.1x | −0.5x | |
PEG Ratio | −0.59 | −0.06 | 0.00 | |
Price/Book | 11.0x | 2.3x | 2.6x | |
Price / LTM Sales | 6.8x | 10.1x | 3.3x | |
Upside (Analyst Target) | 39.4% | 297.7% | 45.1% | |
Fair Value Upside | Unlock | 27.1% | 7.4% | Unlock |