REGENXBIO Inc., a clinical-stage biotechnology company, provides gene therapies that deliver functional genes to cells with genetic defects in the United States. Its gene therapy product candidates are based on NAV Technology Platform, a proprietary adeno-associated virus gene delivery platform. The company’s products in pipeline includes ABBV-RGX-314 for the treatment of wet age-related macular degeneration, diabetic retinopathy, and other chronic retinal diseases; and RGX-202, which is in Phase III clinical trial for the treatment of Duchenne muscular dystrophy, as well as RGX-121 for the treatment of mucopolysaccharidosis type II. It also develops RGX-111 for the treatment of mucopolysaccharidosis type I, RGX-181 for the treatment of late-infantile neuronal ceroid lipofuscinosis type 2, and RGX-381 for the treatment of the ocular manifestations of CLN2 disease. In addition, the company licenses its NAV Technology Platform to other biotechnology and pharmaceutical companies. Further, it has a collaboration and license agreement with AbbVie Global Enterprises Ltd. to develop ABBV-RGX-314 outside the United States. REGENXBIO Inc. was incorporated in 2008 and is headquartered in Rockville, Maryland.
Gene Therapy Pionee | REGENXBIO's innovative AAV platform targets genetic and rare diseases, with promising developments in DMD, wet AMD, and MPS II treatments |
DMD Market Potential | Explore REGENXBIO's RGX-202 gene therapy for Duchenne muscular dystrophy, offering higher expression levels and broader patient eligibility than competitors |
Ocular Breakthroughs | Delve into REGENXBIO's partnership with AbbVie for ocular gene therapies, with pivotal trials and BLA submissions expected in the near future |
Financial Outlook | Analyst price targets range from $13 to $52, suggesting significant upside potential despite current unprofitability and a market cap of $487 million |
Metrics to compare | RGNX | Sector Sector - Average of metrics from a broad group of related Healthcare sector companies | Relationship RelationshipRGNXPeersSector | |
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P/E Ratio | −2.3x | −3.3x | −0.5x | |
PEG Ratio | −0.07 | −0.07 | 0.00 | |
Price/Book | 1.9x | 2.1x | 2.6x | |
Price / LTM Sales | 2.6x | 6.3x | 3.3x | |
Upside (Analyst Target) | 288.9% | 124.6% | 41.6% | |
Fair Value Upside | Unlock | −6.3% | 5.9% | Unlock |