Solid Biosciences Inc. develops therapies for neuromuscular and cardiac diseases in the United States. The company’s lead product candidate is SGT-003, which is in phase 1/2 for the treatment of Duchenne muscular dystrophy. It also develops SGT-212 for the treatment of Friedreich's ataxia that is in phase 1b clinical trial; SGT-501 for the treatment of catecholaminergic polymorphic ventricular tachycardia that is in preclinical phase; SGT-601 the treatment of TNNT2-mediated dilated cardiomyopathy, which is in preclinical phase; SGT-401 for the treatment of BAG3-mediated dilated cardiomyopathy that is in preclinical phase; SGT-701 for treatment of rare inherited disease characterized by mutations in the RBM20 gene, which is in discovery phase; and other drugs for the treatment of cardiac and other diseases. In addition, the company is involved in developing platform technologies, including capsid libraries; genetic regulators, such as promoters, UTRs, and introns; immunomodulation technologies; manufacturing purity; and dual gene expression, a technology for packaging multiple transgenes into one capsid. The company has collaboration and license agreement with Ultragenyx Pharmaceutical Inc.; and a license agreement with the University of Washington, University of Missouri, University of Florida, and ICS Maugeri S.p.A. Solid Biosciences Inc. was incorporated in 2013 and is headquartered in Charlestown, Massachusetts.
Gene Therapy Pionee | Solid Biosciences leads in DMD treatment with SGT-003, showing 100% microdystrophin expression and favorable safety profile in early trials |
Pipeline Expansion | Explore Solid's strategic move into Friedreich's ataxia and CPVT, diversifying its portfolio and tapping into new market opportunities |
Financial Outlook | Delve into Solid's $200M capital raise, extending cash runway to 2027, while analysts set price targets ranging from $10 to $20 |
Market Challenges | Learn how Solid navigates a competitive landscape, regulatory hurdles, and potential safety concerns in the evolving gene therapy field |
Metrics to compare | SLDB | Sector Sector - Average of metrics from a broad group of related Healthcare sector companies | Relationship RelationshipSLDBPeersSector | |
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P/E Ratio | −3.0x | −3.2x | −0.5x | |
PEG Ratio | −0.19 | 0.02 | 0.00 | |
Price/Book | 1.8x | 2.6x | 2.6x | |
Price / LTM Sales | - | 5.8x | 3.3x | |
Upside (Analyst Target) | 142.5% | 203.0% | 40.6% | |
Fair Value Upside | Unlock | −3.6% | 5.3% | Unlock |